September 10, 2025
OXFORD, UK and CLEVELAND, Ohio, US, 10 September 2025 – The Oxford-Harrington Rare Disease Centre (‘OHC’), a partnership between the University of Oxford, UK and Harrington Discovery Institute at University Hospitals, Cleveland, Ohio, dedicated to creating new medicines for rare diseases, announces that Lord...
Continue ReadingJuly 09, 2025
Experimental Compound Offers Potential Treatment for Rare, Often Fatal, Childhood Disease Continue Reading
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The former prime minister has called for children admitted to paediatric care to undergo genome sequencing as part of a drive to cure 40 rare diseases Continue Reading
May 21, 2025
Alzheimer’s disease (AD) and traumatic brain injury (TBI) are currently untreatable neurodegenerative disorders afflicting millions of people worldwide. These conditions are pathologically related, and TBI is one of the greatest risk factors for AD. Continue Reading
January 27, 2025
At 18 weeks pregnant, Lindsey learned her baby had severe spina bifida. She joined UC Davis’s groundbreaking CuRe Trial combining fetal surgery and stem cells. Over a year later, her son is thriving. Continue Reading
December 11, 2024
An off-the-shelf drug shows promise as a low-cost topical treatment for psoriasis. New findings highlight benzamil’s potential to reduce inflammation and skin cell overgrowth without steroids or immune suppression. Continue Reading
September 17, 2024
Progression of acute TBI to chronic neurodegeneration is a major health problem with no protective treatments. Time sensitive inhibition of acutely elevated mitochondrial fission may present a way to protect patients from chronic neurodegeneration. Continue Reading
July 16, 2024
There’s only one U.S. Food and Drug Administration-approved therapy for an inherited retinal disease, and dozens of retinitis pigmentosa (RP) genes for which no therapy is available. Continue Reading
March 25, 2024
Nature Chemical Biology, published March 25, 2024 Continue Reading
March 13, 2024
The rapidly evolving SARS-CoV-2 virus threatens the progress made in curbing the COVID-19 pandemic. A promising novel drug candidate, designed at the atomic level, could help doctors halt the rise of lethal new drug resistant variants. Continue Reading
January 16, 2024
The Jenner Institute is conducting a new study, using BCG, the current licensed vaccine against tuberculosis. Continue Reading